Safety and Efficacy of the Lentiviral Vector in Gene Therapy of Beta-thalassemia Patients

על הניסוי

This is a non-randomized, open-label, single-dose study. The aim of this study is to evaluate the safety and efficacy of the treatment with lentiviral vector encoding βA-T87Q-globin gene transduced autologous hematopoietic stem cells transfusion in subjects with transfusion-dependent β-thalassemia.

צפו ב-NCT06219239 ב-ClinicalTrials.gov ←

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