PF-AtlasClinical Trials › NCT04509050

Study to Evaluate Biological & Clinical Effects of Significantly Corrected CFTR Function in Infants & Young Children

Ivacaftor or elexacaftor/tezacaftor/ivacaftor · Not specified

Registry ID
NCT04509050
Phase
Not specified
Status
Recruiting
Drug / intervention
Ivacaftor or elexacaftor/tezacaftor/ivacaftor
Sponsor
Sonya Heltshe
Start
2020-11-18
Enrollment
210
Locations
35

About this trial

This is a two-part, multi-center, prospective longitudinal, exploratory study of highly effective cystic fibrosis transmembrane conductance regulator (CFTR) modulators and their impact on children with cystic fibrosis (CF).

View NCT04509050 on ClinicalTrials.gov →

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Medical disclaimer. This page summarizes public trial data for NCT04509050 for information only. It is not medical advice, an endorsement, or an offer to enroll. Confirm details on ClinicalTrials.gov and with a qualified physician.