PF-Atlas › Clinical Trials › NCT01621867
Repeated Application of Gene Therapy in CF Patients
pGM169/GL67A · Phase 2
Registry ID
NCT01621867
Phase
Phase 2
Status
Completed
Drug / intervention
pGM169/GL67A
Sponsor
Imperial College London
Start
2012-05
Enrollment
130
Locations
3
About this trial
Cystic fibrosis is a genetic condition where epithelial cells, including from the respiratory tract, have an abnormal function of a surface protein, the cystic fibrosis transmembrane conductance regulator (CFTR) protein resulting from abnormal gene expression. The trial will assess the clinical efficacy, safety \& tolerability and gene expression following repeated nebulised doses of a gene product coding for a normal CFTR protein, with the primary outcome of the trial assessing lung function.
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Medical disclaimer. This page summarizes public trial data for NCT01621867 for information only. It is not medical advice, an endorsement, or an offer to enroll. Confirm details on ClinicalTrials.gov and with a qualified physician.